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Issue Date
Title
Author(s)
2014
Correction of methylmalonic aciduria in vivo using a codon-optimized lentiviral vector
Wong, E.
;
McIntyre, C.
;
Peters, H.
;
Ranieri, E.
;
Anson, D.
;
Fletcher, J.
2014
Lentiviral-mediated gene therapy results in sustained expression of β-Glucuronidase for up to 12 Months in the Gus mps/mps and up to 18 Months in the Gus tm(L175F)Sly mouse models of mucopolysaccharidosis type VII
Derrick-Roberts, A.
;
Pyragius, C.
;
Kaidonis, X.
;
Jackson, M.
;
Anson, D.
;
Byers, S.
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Author
1
Byers, S.
1
Derrick-Roberts, A.
1
Fletcher, J.
1
Jackson, M.
1
Kaidonis, X.
1
McIntyre, C.
1
Peters, H.
1
Pyragius, C.
1
Ranieri, E.
1
Wong, E.
.
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Subject
2
Genetic Therapy
2
Genetic Vectors
2
Lentivirus
2
Liver
1
Amino Acid Metabolism, Inborn Errors
1
Analysis of Variance
1
Bone Density
1
Codon
1
Disease Models, Animal
1
Exploratory Behavior
.
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