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PreviewIssue DateTitleAuthor(s)
2002Phenotypic rescue after adeno-associated virus-mediated delivery of 4-sulfatase to the retinal pigment epithelium of feline mucopolysaccharidosis VIHo, T.; Maguire, A.; Aguirre, G.; Surace, E.; Anand, V.; Zeng, Y.; Salvetti, A.; Hopwood, J.; Haskins, M.; Bennett, J.
2010Lessons learnt from animal models: pathophysiology of neuropathic lysosomal storage disordersHemsley, K.; Hopwood, J.
1999Autologous transplantation of retrovirally transduced bone marrow or neonatal blood cells into cats can lead to long-term engraftment in the absence of myeloablationSimonaro, C.; Haskins, M.; Abkowitz, J.; Brooks, D.; Hopwood, J.; Zhang, J.B.; Schuchman, E.
1996Feline mucopolysaccharidosis type VI - characterization of recombinant N-acetylgalactosamine 4-sulfatase and identification of a mutation causing the diseaseYogalingam, G.; Litjens, T.; Bielicki, J.; Crawley, A.; Muller, V.; Anson, D.; Hopwood, J.
1999Advantages of using same species enzyme for replacement therapy in a feline model of mucopolysaccharidosis type VIBielicki, J.; Crawley, A.; Davey, R.; Varnai, J.; Hopwood, J.
2007Long-term intra-articular administration of recombinant human N-acetylgalactosamine-4-sulfatase in feline mucopolysaccharidosis VIAuclair, D.; Hopwood, J.; Lemontt, J.; Chen, L.; Byers, S.
2012Neonatal gene therapy with a gamma retroviral vector in mucopolysaccharidosis VI catsPonder, K.; O'Malley, T.; Wang, P.; O'Donnell, P.; Traas, A.; Knox, V.; Aguirre, G.; Ellinwood, N.; Metcalf, J.; Wang, B.; Parkinson-Lawrence, E.; Sleeper, M.; Brooks, D.; Hopwood, J.; Haskins, M.
1999Regulation of N-acetylgalactosamine 4-sulfatase expression in retrovirus-transduced feline mucopolysaccharidosis type VI muscle cellsYogalingam, G.; Muller, V.; Hopwood, J.; Anson, D.
2003Replacement therapy in Mucopolysaccharidosis type VI: advantages of early onset of therapyAuclair, D.; Hopwood, J.; Brooks, D.; Lemontt, J.; Crawley, A.
2012Intrathecal recombinant human 4-sulfatase reduces accumulation of glycosaminoglycans in dura of mucopolysaccharidosis VI catsAuclair, D.; Finnie, J.; Walkley, S.; White, J.; Nielsen, T.; Fuller, M.; Cheng, A.; O'Neill, C.; Hopwood, J.