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Preview	Issue Date	Title	Author(s)
	2004	Enzyme replacement therapy in mucopolysaccharidosis VI (Maroteaux-Lamy Syndrome)	Harmatz, P.; Whitley, C.; Waber, L.; Pais, R.; Steiner, R.; Plecko, B.; Kaplan, P.; Simon, J.; Butensky, E.; Hopwood, J.
	2002	Phenotypic rescue after adeno-associated virus-mediated delivery of 4-sulfatase to the retinal pigment epithelium of feline mucopolysaccharidosis VI	Ho, T.; Maguire, A.; Aguirre, G.; Surace, E.; Anand, V.; Zeng, Y.; Salvetti, A.; Hopwood, J.; Haskins, M.; Bennett, J.
	2005	Threshold effect of urinary glycosaminoglycans and the walk test as indicators of disease progression in a survey of subjects with mucopolysaccharidosis VI (Maroteaux-Lamy syndrome)	Swiedler, S.; Beck, M.; Bajbouj, M.; Giugliani, R.; Schwartz, I.; Harmatz, P.; Wraith, J.; Roberts, J.; Ketteridge, D.; Hopwood, J.; Guffon, N.; Miranda, C.; Teles, E.; Berger, K.; Piscia-Nichols, C.
	2001	Mucopolysaccharidosis type VI: Structural and clinical implications of mutations in N-acetylgalactosamine-4-sulfatase	Litjens, T.; Hopwood, J.
	2005	An index case for the attenuated end of the mucopolysaccharidosis type VI clinical spectrum	Brooks, D.; Gibson, G.; Karageorgos, L.; Hein, L.; Robertson, E.; Hopwood, J.
	2007	Long-term intra-articular administration of recombinant human N-acetylgalactosamine-4-sulfatase in feline mucopolysaccharidosis VI	Auclair, D.; Hopwood, J.; Lemontt, J.; Chen, L.; Byers, S.
	2008	Maroteaux-Lamy syndrome: Functional characterization of pathogenic mutations and polymorphisms in the arylsulfatase B gene	Garrido, E.; Cormand, B.; Hopwood, J.; Chabas, A.; Grinberg, D.; Vilageliu, L.
	2002	Mucopolysaccharidosis type VI (Maroteaux-Lamy syndrome): A Y210C mutation causes either altered protein handling or altered protein function of N-acetylgalactosamine 4-sulfatase at multiple points in the vacuolar network	Bradford, T.; Litjens, T.; Parkinson, E.; Hopwood, J.; Brooks, D.
	2003	Replacement therapy in Mucopolysaccharidosis type VI: advantages of early onset of therapy	Auclair, D.; Hopwood, J.; Brooks, D.; Lemontt, J.; Crawley, A.
	2008	Long-term follow-up of endurance and safety outcomes during enzyme replacement therapy for mucopolysaccharidosis VI: Final results of three clinical studies of recombinant human N-acetylgalactosamine 4-sulfatase	Harmatz, P.; Giugliani, R.; Schwartz, I.; Guffon, N.; Teles, E.; Miranda, C.; Wraith, J.; Beck, M.; Arash, L.; Scarpa, M.; Ketteridge, D.; Hopwood, J.; Plecko, B.; Steiner, R.; Whitley, C.; Kaplan, P.; Yu, Z.; Swiedler, S.; Decker, C.